Explore rare diseases in clinical trials

Check which rare diseases are currently being frequently studied.

See also our popular diseases glossary and drug database.

Starting by letter

To open the rare diseases glossary, select a letter from the list below.

Rare diseases starting with “w”

  • 7

    Waldenstrom’s macroglobulinaemia

    Waldenstrom’s macroglobulinaemia is a rare, slow-growing blood cancer that affects white blood cells and causes production of an abnormal protein that can thicken the blood, making it harder to flow through blood vessels.

  • 1

    Waldenstrom’s macroglobulinaemia recurrent

    Waldenstrom’s macroglobulinaemia is a rare blood cancer that cannot be completely cured, which means that after successful treatment, the disease will eventually return. Understanding what happens when the cancer comes back and knowing your treatment options can help you manage this condition effectively.

  • 3

    Waldenstrom’s macroglobulinaemia refractory

    When Waldenstrom’s macroglobulinemia comes back after treatment or stops responding to therapy, patients and their healthcare teams face new decisions about the best path forward.

  • 2

    Wiskott-Aldrich syndrome

    Wiskott-Aldrich syndrome is a rare genetic condition that disrupts the immune system, causes dangerous bleeding problems, and leads to persistent eczema. Without proper treatment, this inherited disorder can become life-threatening, but modern medical advances offer hope through stem cell transplantation and gene therapy.

  • 2

    Wolfram syndrome

    Wolfram syndrome is a rare genetic condition that damages multiple body systems over time, usually beginning with diabetes and vision problems in childhood and progressing to affect the brain and other organs.