Explore rare diseases in clinical trials
Check which rare diseases are currently being frequently studied.
See also our popular diseases glossary and drug database.
Starting by letter
To open the rare diseases glossary, select a letter from the list below.
Rare diseases starting with “w”
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Waldenstrom’s macroglobulinaemia
Waldenstrom’s macroglobulinaemia is a rare, slow-growing blood cancer that affects white blood cells and causes production of an abnormal protein that can thicken the blood, making it harder to flow through blood vessels.
- 1
Waldenstrom’s macroglobulinaemia recurrent
Waldenstrom’s macroglobulinaemia is a rare blood cancer that cannot be completely cured, which means that after successful treatment, the disease will eventually return. Understanding what happens when the cancer comes back and knowing your treatment options can help you manage this condition effectively.
- 3
Waldenstrom’s macroglobulinaemia refractory
When Waldenstrom’s macroglobulinemia comes back after treatment or stops responding to therapy, patients and their healthcare teams face new decisions about the best path forward.
- 2
Wiskott-Aldrich syndrome
Wiskott-Aldrich syndrome is a rare genetic condition that disrupts the immune system, causes dangerous bleeding problems, and leads to persistent eczema. Without proper treatment, this inherited disorder can become life-threatening, but modern medical advances offer hope through stem cell transplantation and gene therapy.
- 2
Wolfram syndrome
Wolfram syndrome is a rare genetic condition that damages multiple body systems over time, usually beginning with diabetes and vision problems in childhood and progressing to affect the brain and other organs.


