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Phelan-McDermid syndrome

  • 1 clinical trial
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1 Clinical trial

Phelan-McDermid syndrome

Not yet recruiting

Study of the Safety, Tolerability and Efficacy of Oral Vafidemstat in Adults with Phelan‑McDermid Syndrome (HOPE‑2)

InvestigationalNo placebo
Countries:SpainSpain
  • Participants:18–64 years
  • Substances:Vafidemstat
  • Sponsor:Oryzon Genomics S.A.
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