Not recruiting
Leukocyte adhesion deficiency+1
Not recruitingStudy on Long-Term Safety and Efficacy of Gene Therapy for Leukocyte Adhesion Deficiency-I Using RP-L201 in Patients with LAD-I
InvestigationalNo placebo
Study on Long-Term Safety and Efficacy of Gene Therapy for Leukocyte Adhesion Deficiency-I Using RP-L201 in Patients with LAD-I
InvestigationalNo placebo
- Disease:Leukocyte adhesion deficiencyLeukocyte adhesion deficiency type I
- Substances:–
Countries:
Spain
Spain- Participants:0–17 years · 18–64 years
- Sponsor:Rocket Pharmaceuticals Inc.
