Recruiting
Hereditary spastic paraplegia
RecruitingPhase IIb Open‑Label Study of Intrathecal Melpida (AAV9/AP4M1) in Patients with Hereditary Spastic Paraplegia Type 50 (SPG50)
InvestigationalNo placebo
Phase IIb Open‑Label Study of Intrathecal Melpida (AAV9/AP4M1) in Patients with Hereditary Spastic Paraplegia Type 50 (SPG50)
InvestigationalNo placebo
- Disease:Hereditary spastic paraplegia
- Substances:Melpida
Countries:
Denmark
Denmark- Participants:0–17 years
- Substances:Melpida
- Sponsor:Elpida Therapeutics SPC


