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recruiting
3 975
countries
28
conditions
2 106

35 trials match your criteria

Chronic graft versus host disease

Recruiting

Study of belumosudil versus drug combination in patients aged 12 years and older with chronic graft‑versus‑host disease refractory after prior therapy

Registered drugNo placebo
Countries:AustriaAustria
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Bortezomib

Adenomatous polyposis coli

Recruiting

A study testing sirolimus to slow disease progression in patients with familial adenomatous polyposis

Investigational
Countries:DenmarkDenmark
  • Participants:18–64 years · 65+ years
  • Substances:Sirolimus

Familial dilated cardiomyopathy

Recruiting

Study of ALXN2350 gene therapy in adults with BAG3 mutation-associated dilated cardiomyopathy: A safety and efficacy trial

Registered drugNo placebo
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years
  • Substances:AAV9-CTNT-COBAG3

Renal transplant

Recruiting

Study of immunosuppression reduction in kidney transplant patients with septic shock or respiratory failure receiving drug combination therapy in intensive care

Registered drugNo placebo
Countries:FranceFrance
  • Participants:18–64 years · 65+ years
  • Substances:Azathioprine

Chronic kidney disease

Recruiting

Study on Tacrolimus and Sirolimus for Kidney Transplant Patients at High Risk of Cytomegalovirus Infection

Registered drugNo placebo
Countries:SpainSpain
  • Participants:18–64 years · 65+ years
  • Substances:Mycophenolic Acid

Naevus flammeus

Recruiting

Study on the Effects of Sirolimus Cream for Patients with Port Wine Stains

Registered drug
Countries:SpainSpain
  • Participants:0–17 years · 18–64 years
  • Substances:Sirolimus

Tuberous sclerosis complex+1

Recruiting

Study on the Safety and Effectiveness of Sirolimus and Vigabatrin for Preventing Symptoms in Infants with Tuberous Sclerosis Complex

Registered drug
Countries:PolandPoland
  • Participants:0–17 years
  • Substances:Sirolimus

Tuberous sclerosis complex+1

Recruiting

Study on the Effectiveness and Safety of Sirolimus for Patients with Drug-Resistant Epilepsy Linked to Tuberous Sclerosis Complex

Registered drug
Countries:PolandPoland
  • Participants:0–17 years · 18–64 years
  • Substances:Sirolimus

Brain stem glioma

Recruiting

Study on the Effectiveness of Sirolimus and Trametinib for Treating Diffuse Intrinsic Pontine Glioma in Children Aged 3-18 Years

Registered drugNo placebo
Countries:PolandPoland
  • Participants:0–17 years · 18–64 years
  • Substances:Sirolimus

Crigler-Najjar syndrome

Recruiting

Study of GNT0003 and imlifidase in adults with Crigler-Najjar syndrome who require daily phototherapy and have pre-existing AAV8 antibodies

Registered drugNo placebo
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Amoxicillin Sodium

Acute myeloid leukaemia

Recruiting

Study on Cyclophosphamide and Etoposide with Radiation for High-Risk Myelodysplastic Syndrome or Acute Myeloid Leukemia Patients Preparing for Transplant

Registered drugNo placebo
Countries:SpainSpain
  • Participants:18–64 years · 65+ years
  • Substances:Cyclophosphamide

Endocrine ophthalmopathy

Recruiting

Study Comparing Sirolimus and Methylprednisolone for Patients with Active Thyroid Eye Disease

Registered drugNo placebo
Countries:NorwayNorway
  • Participants:18–64 years · 65+ years
  • Substances:Methylprednisolone

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