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recruiting
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2 trials match your criteria

Fabry's disease

Recruiting

Study on the Safety and Effects of Pegunigalsidase Alfa for Children and Adolescents with Fabry Disease

InvestigationalNo placebo
Countries:AustriaAustria
  • Participants:0–17 years
  • Substances:Pegunigalsidase Alfa

Fabry's disease

Not recruiting

Study on the Long-Term Safety and Effectiveness of Pegunigalsidase Alfa for Adults with Fabry Disease

InvestigationalNo placebo
Countries:BelgiumBelgium
  • Participants:18–64 years
  • Substances:Pegunigalsidase Alfa
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