Rare diseases
Investigational molecules
Locations
Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of DNL952 in Adults with Late‑Onset Pompe Disease
GermanySensitivity and specificity of Lepidoglyphus destructor extract, sodium chloride and histamine dihydrochloride in skin prick test for Lepidoglyphus destructor allergy patients
SpainEvaluation of NXT007 versus Emicizumab Prophylaxis in Patients with Hemophilia A
AustriaA Phase III study of NXT007 compared with simoctocog alfa prophylaxis in patients with Hemophilia A without inhibitors
AustriaStudy of Fludeoxyglucose (18F) PET Imaging of Brain Metabolism in Patients with Persistent Post‑COVID Syndrome
The NetherlandsSafety and effectiveness of ponatinib and asciminib in chronic myeloid leukemia patients resistant to these drugs
SpainEfficacy and safety of indacaterol acetate (combined with glycopyrronium bromide and mometasone furoate) versus salmeterol/fluticasone in adolescents with asthma
FranceLidocaine Hydrochloride, Sodium Chloride, and Betamethasone Injections for Adults with Adhesive Capsulitis: A Pilot Efficacy Study
FranceStudy of nivolumab plus drug combination versus standard first-line therapy in patients with advanced Hodgkin lymphoma
PolandLong‑Term Safety and Tolerability of KarXT in Adolescents with Schizophrenia and of KarXT + KarX‑EC in Children and Adolescents with Autism‑Related Irritability
RomaniaPhase 2 Randomized Study of Povetacicept to Assess Safety and Effectiveness in Adults with Generalized Myasthenia Gravis
PolandShort‑course sublingual ITULAZAX birch pollen extract with Lactobacillus rhamnosus GG for patients with pollen‑associated food allergy
GermanyTell us about your condition – we search every trial in Europe and connect you with the right site.
