Not yet recruiting
Homocystinuria
Not yet recruitingSafety and Tolerability Study of Subcutaneous Pegtibatinase in Adults and Children with Classical Homocystinuria (Phase 1/2)
InvestigationalNo placebo
Safety and Tolerability Study of Subcutaneous Pegtibatinase in Adults and Children with Classical Homocystinuria (Phase 1/2)
InvestigationalNo placebo
- Disease:Homocystinuria
- Substances:Pegtibatinase
Countries:
France
France- Participants:0–17 years · 18–64 years · 65+ years
- Substances:Pegtibatinase
- Sponsor:Travere Therapeutics Inc.
