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Solid Biosciences Inc.
Sponsor

Solid Biosciences Inc.

United States 500 Rutherford Avenue, 02129-1647, United States

About the sponsor

Solid Biosciences Inc. focuses on neuromuscular disease research, with activity centered on Duchenne muscular dystrophy and the development of gene therapy approaches aimed at restoring microdystrophin expression in muscle tissue.

  • Muscle biopsy biomarker assessment
  • Microdystrophin expression
  • Intravenous gene delivery

The sponsor’s clinical research interest is concentrated on treatment strategies for the genetic basis of Duchenne muscular dystrophy, with emphasis on skeletal muscle function and disease-related protein restoration.

About Specializations

Solid Biosciences Inc. runs clinical trials in conditions such as Duchenne muscular dystrophy, among others.

Recruiting now

Ongoing trials

Clinical trials run by this sponsor – those enrolling participants first.

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Quick filters

2 clinical trials

Countries:ItalyItaly
  • Participants:0–17 years
  • Substances:SGT-003
  • Sponsor:Solid Biosciences Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years
  • Substances:SGT-003
  • Sponsor:Solid Biosciences Inc.

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