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San Raffaele Hospital

Italy Via Olgettina 58, 20132 Milan, Italy

About the sponsor

Clinical research activity includes transfusion-dependent beta-thalassemia, with attention to restoring transfusion independence and improving outcomes in patients with chronic haemoglobin disorders.

  • Beta-thalassemia
  • Transfusion dependence
  • Haematopoietic stem cell therapy

The sponsor’s work in this area is centred on gene therapy approaches for inherited anaemias and related blood-cell replacement strategies.

About Specializations

San Raffaele Hospital runs clinical trials in conditions such as Thalassaemia beta, Thalassaemia, Osteopetrosis, Primary immunodeficiency syndrome, among others.

Recruiting now

Ongoing trials

Clinical trials run by this sponsor – those enrolling participants first.

Condition
Country
City
Type of trial
Recruitment status
Quick filters

3 clinical trials

Thalassaemia beta+1

Recruiting

A Study of Gene Therapy Using Modified Stem Cells for Patients with Transfusion-Dependent Beta-Thalassemia Who Need Regular Blood Transfusions

Registered drugNo placebo
Countries:ItalyItaly
  • Participants:0–17 years · 18–64 years
  • Substances:Busulfan
  • Sponsor:Fondazione Telethon Ets

Osteopetrosis

Recruiting

Study of gene-modified stem cells (FT024) in children with TCIRG1-related osteopetrosis using treosulfan, thiotepa, and plerixafor for treatment

Registered drugNo placebo
Countries:ItalyItaly
  • Participants:0–17 years
  • Substances:Plerixafor
  • Sponsor:Fondazione Telethon Ets

Primary immunodeficiency syndrome

Not yet recruiting

Autologous CD4+ T-Cell Gene Therapy for X-linked Hyper-IgM Syndrome Type 1 in Patients with X-linked Hyper-IgM Syndrome Type 1

Registered drugNo placebo
Countries:ItalyItaly
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Diphtheria toxoid adsorbed on aluminium hydroxide, hydrated
  • Sponsor:Fondazione Telethon Ets

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