Long-Term Safety and Efficacy of KL1333 in Adults with Primary Mitochondrial Disease
Belgium- Participants:18–64 years · 65+ years
- Substances:2-Isopropyl-3H-Naphtho(1,2-D)Imidazole-4,5-Dione
- Sponsor:Pharming Technologies B.V.
Rare diseases
Investigational molecules
Locations

Darwinweg 24, 2333 CR Leiden, The Netherlands
Pharming Technologies B.V. focuses clinical research on primary immunodeficiency disorders, with particular attention to common variable immunodeficiency and related immune dysregulation conditions. Its studies address the clinical burden of abnormal immune function in both adult and pediatric populations.
Research in this area includes ongoing work in patients with clinically significant immune dysfunction across multiple age groups.
Pharming Technologies B.V. runs clinical trials in conditions such as Activated PI3 kinase delta syndrome, Immunodeficiency common variable, Primary immunodeficiency syndrome, among others.
Clinical trials run by this sponsor – those enrolling participants first.
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