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Genetix Biotherapeutics Inc.
Sponsor

Genetix Biotherapeutics Inc.

United States 455 Grand Union Boulevard, 02145-1446, United States

About the sponsor

Genetix Biotherapeutics Inc. supports clinical research in inherited blood diseases, with particular attention to sickle-cell disease and beta-thalassaemia. Its studies focus on long-term outcomes in people living with chronic haemoglobinopathies that affect oxygen transport and blood cell production.

  • Sickle-cell disease
  • Beta-thalassaemia
  • Transfusion-dependent thalassaemia

The research emphasis includes sustained monitoring of safety and effectiveness in individuals treated for severe inherited anaemias.

About Specializations

Genetix Biotherapeutics Inc. runs clinical trials in conditions such as Sickle cell disease, Adrenoleukodystrophy, Thalassaemia beta, among others.

Recruiting now

Ongoing trials

Clinical trials run by this sponsor – those enrolling participants first.

Condition
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Type of trial
Recruitment status
Quick filters

3 clinical trials

Sickle cell disease

Recruiting

Long-term Safety and Efficacy Study of Lovotibeglogene Autotemcel Gene Therapy for Patients with Sickle Cell Disease

InvestigationalNo placebo
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Substances:Lovotibeglogene Autotemcel
  • Sponsor:Genetix Biotherapeutics Inc.

Adrenoleukodystrophy

Not recruiting

Long-term Safety and Efficacy Study of Elivaldogene Autotemcel for Patients with Cerebral Adrenoleukodystrophy

InvestigationalNo placebo
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Elivaldogene Autotemcel
  • Sponsor:Genetix Biotherapeutics Inc.

Thalassaemia beta

Not recruiting

Long-Term Safety and Efficacy Study of Betibeglogene Autotemcel Gene Therapy for Patients with Transfusion-Dependent Beta-Thalassemia

InvestigationalNo placebo
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Substances:Betibeglogene Autotemcel
  • Sponsor:Genetix Biotherapeutics Inc.

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