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Dyne Therapeutics Inc.
Sponsor

Dyne Therapeutics Inc.

United States 1560 Trapelo Road, 02451-7306, United States

About the sponsor

Clinical research in Duchenne muscular dystrophy focuses on muscle disease affecting strength and mobility, with attention to restoring dystrophin expression in skeletal muscle tissue.

  • Muscle function
  • Dystrophin protein
  • Skeletal muscle involvement

These studies examine therapeutic interest in progressive neuromuscular impairment and the biological markers linked to muscle integrity.

About Specializations

Dyne Therapeutics Inc. runs clinical trials in conditions such as Myotonic dystrophy, Duchenne muscular dystrophy, among others.

Recruiting now

Ongoing trials

Clinical trials run by this sponsor – those enrolling participants first.

Condition
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Quick filters

3 clinical trials

Registered drug
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Substances:Humanised Igg1 Kappa Fragment Antibody Targeting Tfr1 Conjugated To P125 Oligonucleotide
  • Sponsor:Dyne Therapeutics Inc.

Myotonic dystrophy

Not recruiting
Investigational
Countries:FranceFrance
  • Participants:18–64 years
  • Substances:Humanised Igg1 Kappa Fragment Antibody Targeting Tfr1 Conjugated To P125 Oligonucleotide
  • Sponsor:Dyne Therapeutics Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years
  • Substances:Fragment Antibody Targeting Human Tfr1 Conjugated To Phosphorodiamidate Morpholino Oligomer
  • Sponsor:Dyne Therapeutics Inc.

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