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Biocryst Pharmaceuticals Inc.
Sponsor

Biocryst Pharmaceuticals Inc.

United States 4505 Emperor Boulevard Suite 200, 27703-8457, United States

About the sponsor

Biocryst Pharmaceuticals Inc. focuses on clinical research in hereditary angioedema, with attention to long-term treatment use, ongoing safety evaluation, and symptom control in affected patients.

  • Berotralstat safety
  • Long-term access in HAE
  • Oral therapy for HAE attacks

Its research activity includes both adult and pediatric populations, reflecting interest in treatment continuity across different age groups.

About Specializations

Biocryst Pharmaceuticals Inc. runs clinical trials in conditions such as Hereditary angioedema, Netherton's syndrome, among others.

Recruiting now

Ongoing trials

Clinical trials run by this sponsor – those enrolling participants first.

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3 clinical trials

A Study of BCX17725 Safety and Effects in Healthy People and Patients with Netherton Syndrome

InvestigationalNo placebo
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years
  • Sponsor:Biocryst Pharmaceuticals Inc.

Long-Term Safety Study of Berotralstat for Patients with Hereditary Angioedema from Previous Trials

Registered drugNo placebo
Countries:CzechiaCzechia
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Berotralstat
  • Sponsor:Biocryst Pharmaceuticals Inc.

Hereditary angioedema

Not recruiting

Study on the Safety and Effects of Berotralstat for Children Aged 2 to 12 with Hereditary Angioedema (HAE)

Registered drugNo placebo
Countries:AustriaAustria
  • Participants:0–17 years
  • Substances:Berotralstat
  • Sponsor:Biocryst Pharmaceuticals Inc.

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