Stargardt's disease
RecruitingA study to evaluate the safety and effectiveness of AAVB-039 in patients with Stargardt disease
A study to evaluate the safety and effectiveness of AAVB-039 in patients with Stargardt disease
- Disease:Stargardt's disease
- Substances:COMBINATION OF TWO ADENO-ASSOCIATED VIRAL VECTORS OF SEROTYPE 8 CONTAINING THE 5'- AND THE 3'- HALF CODING SEQUENCES OF HUMAN ABCA4 FUSED TO INTEINS
Belgium- Participants:0–17 years · 18–64 years
- Substances:COMBINATION OF TWO ADENO-ASSOCIATED VIRAL VECTORS OF SEROTYPE 8 CONTAINING THE 5'- AND THE 3'- HALF CODING SEQUENCES OF HUMAN ABCA4 FUSED TO INTEINS
- Sponsor:Aavantgarde Bio S.r.l.



