Rare diseases
Investigational molecules
Locations
Rare diseases with the highest number of active trials right now.
Colours show each disease's body system – lighter shades rank lower.
No. 1 most studied
Shares are of these ten diseases' active trials together.
Browse every rare disease currently studied across European trials.
204 rare diseases
A disease is called rare in the EU when it affects fewer than 5 in 10 000 people. Individually uncommon, together they affect millions – and most still have no approved treatment.
Because the number of patients is small, trials in rare diseases often recruit across several countries at once. That is why a trial listed here may be worth looking at even when it runs nowhere near you.
Tell us about your condition – we search every trial in Europe and connect you with the right site.
