Study on the Safety and Efficacy of Empasiprubart for Adults with Dermatomyositis
GreeceStudy on the Effects of Ribitol (BBP-418) in Patients with Limb Girdle Muscular Dystrophy Type 2I
DenmarkStudy on the Effects of Pariglasgene Brecaparvovec for Adults with Glycogen Storage Disease Type Ia
The NetherlandsStudy on the Effects and Safety of RO7204239 for Patients with Facioscapulohumeral Muscular Dystrophy
DenmarkStudy on the Safety and Efficacy of Viltolarsen for Boys with Duchenne Muscular Dystrophy
CzechiaStudy on Salbutamol for Improving Muscle Strength in Patients with Congenital Myopathy
SwedenSafety and effectiveness study of DYNE-101 in patients with Myotonic Dystrophy Type 1 (DM1)
FranceStudy on the Long-Term Safety and Effectiveness of Losmapimod for Patients with Facioscapulohumeral Muscular Dystrophy (FSHD)
FranceStudy to Determine the Best Dose of Vesleteplirsen for Patients with Duchenne Muscular Dystrophy Suitable for Exon 51-Skipping Treatment
BelgiumStudy of Pariglasgene Brecaparvovec and Prednisolone for Adults with Glycogen Storage Disease Type Ia
DenmarkStudy on the Safety and Effects of mRNA-3745 for Patients with Glycogen Storage Disease Type 1a (GSD1a)
FranceStudy on the Safety and Effects of Losmapimod for Patients with Facioscapulohumeral Muscular Dystrophy 1 (FSHD1)
The Netherlandspowered by
