Study on Anifrolumab for Adults with Polymyositis or Dermatomyositis
FranceDuchenne Muscular Dystrophy in Patients with Gene Mutations Amenable to Exon 44 Skipping Treated with Delpacibart Zotadirsen
FranceA study to evaluate the efficacy and safety of DYNE-101 in patients with Myotonic Dystrophy Type 1
FranceA study to evaluate the safety and effectiveness of surlorian in adults with RYR1-related myopathy
FranceA Study of S-606001 Added to Enzyme Replacement Therapy for Patients with Late-Onset Pompe Disease
FranceA study testing sonlicromanol in adults with genetically confirmed mitochondrial DNA 3243A>G variant causing mitochondrial disease
FranceA Study Testing AOC 1020 to Improve Movement in Adults with Facioscapulohumeral Muscular Dystrophy
FranceStudy of AlloNK and rituximab with cyclophosphamide and fludarabine in adults with relapsing rheumatoid arthritis, inflammatory myopathies, systemic sclerosis, or Sjögren's disease
FranceStudy of intravenous AOC 1001 to evaluate long-term safety and effectiveness in patients with myotonic dystrophy type 1
FranceStudy on Long-Term Safety and Efficacy of VX-670 for Adults with Myotonic Dystrophy Type I
FranceStudy of ENTR-601-45 Safety and Effectiveness in Patients with Duchenne Muscular Dystrophy Who Can Skip Exon 45
FranceStudy of ENTR-601-44 in Children with Duchenne Muscular Dystrophy Who Are Eligible for Exon 44 Skipping Treatment
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