Study of BMN 351 given by intravenous infusion to evaluate safety and tolerability in patients with Duchenne Muscular Dystrophy
SpainStudy on the Effects of Casimersen and Golodirsen for Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Skipping
SpainStudy on the Effectiveness and Safety of Losmapimod for Patients with Facioscapulohumeral Muscular Dystrophy (FSHD)
SpainStudy on the Safety and Effects of Delandistrogene Moxeparvovec in Children Under 4 with Duchenne Muscular Dystrophy
SpainStudy on AOC 1001 for Treating Myotonic Dystrophy Type 1 in Patients
SpainStudy on the Effects and Safety of Efgartigimod PH20 SC for Adults with Active Idiopathic Inflammatory Myopathy
SpainStudy on the Safety and Efficacy of Delandistrogene Moxeparvovec and Imlifidase for Patients with Duchenne Muscular Dystrophy with Pre-existing Antibodies
SpainStudy on the Effects of Satralizumab in Children and Adolescents with Duchenne Muscular Dystrophy
SpainStudy on Long-Term Safety and Effectiveness of Vamorolone in Boys with Duchenne Muscular Dystrophy Who Completed Previous Vamorolone Studies
SpainStudy on Eteplirsen for Patients with Duchenne Muscular Dystrophy with Deletion Mutations Amenable to Exon 51 Skipping
SpainStudy on the Safety and Efficacy of Empasiprubart for Adults with Dermatomyositis
SpainStudy on the Effects of Pariglasgene Brecaparvovec for Adults with Glycogen Storage Disease Type Ia
Spainpowered by
