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56 trials match your criteria

Glycogen storage disease type I

Not recruiting

Study of Pariglasgene Brecaparvovec and Prednisolone for Adults with Glycogen Storage Disease Type Ia

Registered drug
Countries:GermanyGermany
  • Participants:0–17 years · 18–64 years · 65+ years

Glycogen storage disease type II

Not recruiting

Study on the Effectiveness and Safety of Avalglucosidase Alfa for Babies with Infantile-Onset Pompe Disease

Registered drugNo placebo
Countries:GermanyGermany
  • Participants:0–17 years

Duchenne muscular dystrophy

Not recruiting

Study on the Effects of Fordadistrogene Movaparvovec for Patients with Duchenne Muscular Dystrophy

Registered drug
Countries:GermanyGermany
  • Participants:0–17 years

Glycogen storage disease type II

Not recruiting

Study on the Safety and Efficacy of Cipaglucosidase Alfa and Miglustat for Children with Late-onset Pompe Disease

InvestigationalNo placebo
Countries:GermanyGermany
  • Participants:0–17 years

Inclusion body myositis

Not recruiting

Study on the Safety and Effectiveness of ABC008 for Patients with Inclusion Body Myositis

Investigational
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years

Becker's muscular dystrophy

Not recruiting

Study on the Long-term Effects of EDG-5506 for Adults and Adolescents with Becker Muscular Dystrophy

InvestigationalNo placebo
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years

Becker's muscular dystrophy

Not recruiting

Study on the Effects of EDG-5506 for Adults and Adolescents with Becker Muscular Dystrophy

Investigational
Countries:GermanyGermany
  • Participants:18–64 years

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