Rare diseases
Investigational molecules
Locations
459 conditions with trials, the busiest first
1 397 trials across Europe, recruiting first
Study on Long-term Safety and Efficacy of Mexiletine for Children with Myotonic Disorders
FranceStudy on the Effects of Ribitol (BBP-418) in Patients with Limb Girdle Muscular Dystrophy Type 2I
DenmarkStudy on the Effects and Safety of Piromelatine for Patients with Idiopathic Rapid Eye Movement Behavior Disorder (iRBD)
AustriaStudy on the Effects of Dimethyl Fumarate for Patients with Adrenomyeloneuropathy
SpainStudy of NIDO-361 for Patients with Spinal and Bulbar Muscular Atrophy (SBMA)
DenmarkStudy on the Effects of Satralizumab for Patients with Myelin Oligodendrocyte Glycoprotein Antibody-Associated Disease (MOGAD)
FranceStudy on the Effectiveness and Safety of Ocrelizumab for Adults with Primary Progressive Multiple Sclerosis
BelgiumStudy on the Safety and Effectiveness of Rozanolixizumab in Children with Generalized Myasthenia Gravis
ItalyStudy on the Long-Term Safety of PTC923 (Sepiapterin) for Patients with Phenylketonuria
CzechiaStudy on Long-term Safety and Effects of ARGX-117 for Adults with Multifocal Motor Neuropathy
AustriaStudy on the Safety and Pharmacokinetics of Risdiplam in Infants with Spinal Muscular Atrophy
BelgiumStudy on Bepranemab for Patients with Early Alzheimer's Disease
BelgiumThe therapies tested most often in Nervous system disorders trials.
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