Rare diseases
Investigational molecules
Locations
459 conditions with trials, the busiest first
1 397 trials across Europe, recruiting first
Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of DNL952 in Adults with Late‑Onset Pompe Disease
GermanyLong‑Term Safety and Tolerability of KarXT in Adolescents with Schizophrenia and of KarXT + KarX‑EC in Children and Adolescents with Autism‑Related Irritability
RomaniaPhase 2 Randomized Study of Povetacicept to Assess Safety and Effectiveness in Adults with Generalized Myasthenia Gravis
PolandLong‑Term Safety and Tolerability of Oral Fesoterodine in Adults with Hallucinations and Delusions Due to Alzheimer’s Disease Psychosis
BulgariaIodixanol in Cerebral Angiography for Patients with Unruptured Intracranial Aneurysms
FranceDuchenne Muscular Dystrophy in Patients with Gene Mutations Amenable to Exon 44 Skipping Treated with Delpacibart Zotadirsen
BelgiumRabies Prophylaxis in Healthy Volunteers After Rabies Virus (Inactivated) Strain Flury LEP Vaccination
BelgiumNaxitamab Added to Standard Induction Therapy for Children and Teenagers with Newly Diagnosed High-Risk Neuroblastoma
SpainAUR200 for Patients with Generalized Myasthenia Gravis
DenmarkStudy of Tirabrutinib, Rituximab, and Temozolomide in Patients with Relapsed/Refractory Primary Central Nervous System Lymphoma
AustriaOpen-Label Extension Study of ATH434-DP2 in Patients with Multiple System Atrophy
FranceDaridorexant for Insomnia in Patients with Major Depressive Disorder and Moderate to Severe Insomnia
SpainThe therapies tested most often in Nervous system disorders trials.
Tell us about your condition – we search every trial in Europe and connect you with the right site.
