Study on the Effectiveness and Safety of Nizubaglustat in Patients with Niemann-Pick Type C, GM1, or GM2 Gangliosidosis
- Substances:Nizubaglustat
France- Participants:0–17 years · 18–64 years
- Substances:Nizubaglustat
- Sponsor:Azafaros B.V.
Rare diseases
Investigational molecules
Locations
Back to France3 418 clinical trials in Le Kremlin-Bicetre, France across 2 research sites. Every trial is listed in the EU Clinical Trials Register and updated daily.
Our site in FranceEssaisCliniques.fr(opens in a new tab)
FranceStudy on ICEF15 for Treating Fecal Incontinence in Patients with Anal Sphincter Dysfunction
FranceStudy Comparing Doravirine/Lamivudine and Dolutegravir/Lamivudine for HIV Patients with Controlled Viral Load on Three-Drug Regimens
FranceStudy on Acoramidis for Preventing Transthyretin Amyloidosis in Young People with a Genetic Risk
FranceStudy of deucrictibant tablets for prevention of hereditary angioedema attacks in adults and adolescents
FranceStudy Comparing Sodium Chloride and Sodium Lactate for Treating Severe Diabetic Ketoacidosis in ICU Patients
FranceStudy on Cabozantinib and Nivolumab for Older Patients with Kidney Cancer
FranceStudy on the Effectiveness and Safety of BAY 2927088 for Patients with Advanced Solid Tumors with HER2 Mutations
FranceStudy on Human Albumin Solution and Ringer Lactate for Patients Undergoing Cytoreductive Surgery with Hyperthermic Intraperitoneal Chemotherapy
FranceStudy on the Effects of Testosterone Gel on Physical Performance in Critically Ill Patients Requiring Long-Term Mechanical Ventilation
FranceStudy Comparing BMS-986489 with Chemotherapy to Atezolizumab with Chemotherapy for First-Line Treatment in Patients with Extensive-Stage Small Cell Lung Cancer
FranceStudy on Axatilimab and Corticosteroids for Initial Treatment of Chronic Graft-Versus-Host Disease in Patients
FranceThe busiest research cities in the country
What the registry says about research in the country
Research in this area focuses on bacterial infections, especially severe ear, nose and throat diseases such as idiopathic purulent oedematous sinusitis in adults. The trials are aimed at evaluating whether treatment can improve symptoms and overall patient well-being.
In Kremlin Bicêtre, this work reflects a practical effort to better manage chronic ENT infection-related complaints.
Clinical research here also covers cardiovascular disease in patients hospitalized for septic shock with tachycardia and hypercontractility. The main goal is to evaluate whether controlling heart rate may help improve survival and clinical outcomes.
These trials are designed to clarify whether better cardiovascular support can reduce risk in critically ill patients.
Another key research focus is otorhinolaryngology, with attention on sinusitis and related ENT disorders. The studies are looking at treatment effectiveness and changes in patient-reported symptoms during follow-up.
This area highlights efforts to improve everyday functioning for patients living with ongoing nasal and sinus problems.
Tell us about your condition – we search every trial in Europe and connect you with the right site.