Study on the Safety and Efficacy of Viltolarsen for Boys with Duchenne Muscular Dystrophy
SpainStudy on the Long-Term Safety and Effectiveness of Losmapimod for Patients with Facioscapulohumeral Muscular Dystrophy (FSHD)
SpainStudy to Determine the Best Dose of Vesleteplirsen for Patients with Duchenne Muscular Dystrophy Suitable for Exon 51-Skipping Treatment
SpainStudy of Pariglasgene Brecaparvovec and Prednisolone for Adults with Glycogen Storage Disease Type Ia
SpainStudy on the Safety and Effects of mRNA-3745 for Patients with Glycogen Storage Disease Type 1a (GSD1a)
SpainStudy on the Effectiveness and Safety of Avalglucosidase Alfa for Babies with Infantile-Onset Pompe Disease
SpainStudy of DYNE-251 safety and effectiveness in patients with Duchenne muscular dystrophy who are candidates for exon 51 skipping treatment
SpainStudy on the Effects of Fordadistrogene Movaparvovec for Patients with Duchenne Muscular Dystrophy
SpainStudy on the Long-term Effects of EDG-5506 for Adults and Adolescents with Becker Muscular Dystrophy
SpainStudy on the Effects of EDG-5506 for Adults and Adolescents with Becker Muscular Dystrophy
SpainStudy on the Effects of Enpatoran for Patients with Dermatomyositis and Polymyositis
SpainStudy on the Effects of GLPG3667 for Adults with Dermatomyositis
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