Phase 3 Randomized Double‑Blind Placebo‑Controlled Study of Intravenous sgt-003 in Ambulatory Male Patients with Duchenne Muscular Dystrophy
FranceStudy of ASP2957 Gene Therapy for Male Patients with X-linked Myotubular Myopathy Who Require Breathing Support with Ventilators
FranceStudy on the Effects of Rapcabtagene Autoleucel and Drug Combination for Patients with Severe Refractory Inflammatory Muscle Diseases
FranceStudy on the Safety and Effectiveness of Delandistrogene Moxeparvovec for Patients with Duchenne Muscular Dystrophy
FranceStudy on the Safety of ATA-200 Gene Therapy for Patients with Limb-Girdle Muscular Dystrophy Type R5
FranceStudy on the Effects of Human Normal Immunoglobulin in Adults with Dermatomyositis
FrancePhase 2 Study of Daxdilimab with Prednisone in Adults with Inadequately Controlled Dermatomyositis or Anti‑Synthetase Inflammatory Myositis
FranceTitle: Long-term safety and effectiveness study of ulviprubart in patients with inclusion body myositis who completed previous treatment
FranceStudy on the Effectiveness and Safety of Losmapimod for Patients with Facioscapulohumeral Muscular Dystrophy (FSHD)
FranceStudy on the Safety and Effects of Delandistrogene Moxeparvovec in Children Under 4 with Duchenne Muscular Dystrophy
FranceLong-Term Safety Study of Avalglucosidase Alfa for Patients with Pompe Disease in France
FranceStudy on AOC 1001 for Treating Myotonic Dystrophy Type 1 in Patients
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