Congenital hypotransferrinaemia – European Clinical Trials Information Network https://clinicaltrials.eu Bridging Patients with Clinical Trials Fri, 12 Jun 2026 10:37:11 +0000 en-US hourly 1 https://wordpress.org/?v=7.0 https://clinicaltrials.eu/wp-content/uploads/2024/12/cropped-EU_icon-32x32.png Congenital hypotransferrinaemia – European Clinical Trials Information Network https://clinicaltrials.eu 32 32 Study on the Use of Human Apotransferrin for Treating Patients with Atransferrinemia https://clinicaltrials.eu/trial/study-on-the-use-of-human-apotransferrin-for-treating-patients-with-atransferrinemia/ Wed, 29 Apr 2026 15:01:04 +0000 https://clinicaltrials.eu/trial/study-on-the-use-of-human-apotransferrin-for-treating-patients-with-atransferrinemia/ This clinical trial is focused on studying a rare blood disorder called atransferrinemia. Atransferrinemia is a condition where the body has very low levels of a protein called transferrin, which is important for transporting iron in the blood. The treatment being tested in this study is called Human Apotransferrin, which is given as a solution through an intravenous infusion. This means the treatment is delivered directly into the bloodstream through a vein.

The purpose of the study is to evaluate how the body processes Human Apotransferrin, as well as its effectiveness and safety in treating atransferrinemia. Participants in the study will receive different doses of Human Apotransferrin to find the most effective and safe dose. The study will monitor changes in important blood components, such as hemoglobin and hematocrit, which are indicators of healthy blood function. It will also look at how the treatment affects iron levels in the body, including the liver and heart, to ensure there is no iron overload.

Throughout the study, participants will have regular check-ups to assess their response to the treatment and to monitor any side effects. The study aims to improve the understanding of how Human Apotransferrin can help manage atransferrinemia and improve the quality of life for those affected by this condition.

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